Hunter’s syndrome
- Exploration of IQ as a relevant endpoint in Hunter’s syndrome
- Endpoint review in Hunter’s syndrome
- PRO dossier on the Disease Activity Score (DAS), Scales of Independent Behaviour-Revised (SIB-R), Behaviour Rating Inventory of Executive Function (BRIEF) and Vineland Adaptive Behaviour Scales (VABS) for Hunter’s syndrome
- Strategic PRO and ObsRO analysis of a Hunter’s Syndrome clinical trial database
- Regulatory support for questionnaires in Hunter’s syndrome