Other therapeutic areas

Other publications

Multiple indications

Placement of recall period in patient-reported outcome questionnaire items: Does it matter? 
Mazar I, Taylor F, Higgens S, Shields AL, Carson R, Eremenco S, Reasner DS, Levy-Hacham O, Mizrahi R, Nadler-Milbauer M, Nov O, Toledano O, Coons SJ
Poster session presented at the 22nd Annual International Meeting of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Boston, MA USA, 20-24 May 2017

Qualitative research to explore the patient experience of X-Linked Hypophosphataemia (XLH) and to evaluate the content validity of the BPI-SF and WOMAC® for use as clinical trial endpoints
Theodore-Oklota C, Arbuckle R, Bonner N, Spencer H
Poster presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 22nd Annual International Meeting, Boston, MA USA, 20-24 May 2017

Qualitative research to explore the pediatric patient experience of X-Linked Hypophosphataemia (XLH) and to evaluate the content validity of PROMIS® item banks, FPS-R® and POSNA-PODCI for use as clinical trial endpoints
Theodore-Oklota C, Arbuckle R, Marshall C, Spencer H
Abstract submitted to 10th International Meeting of Pediatric Endocrinology, Washington DC, USA, 14-17 September, 2017

Qualitative research to explore the patient experience of X-Linked Hypophosphatemia and evaluate the suitability of the BPI-SF and WOMAC® as clinical trial endpoints
Theodore-Oklota C, Bonner N, Spencer H, Arbuckle R, Chen C-Y, Skrinar A
Value in Health (accepted for publication)

The burden of relapse on European hematologists treating multiple myeloma
Hansen T, Streetly M, Laurenson S, Lawrence J, Hulin C
Poster session presented at: 19th Congress of the European Haematology Association, Milan, Italy, 12-15 June 2014

The reliability of the patient-reported scar evaluation questionnaire (PR-SEQ) in a cohort of adults with linear scars
Pleil A, Mathias A, Galipeau N, Shields AL, Jensen J
Poster presented at the 19th Annual International Meeting of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR). Montreal, QC Canada

Economic impact of thromboembolism following major orthopedic surgery in Japan
Takai S, Akagi M, Crawford B,  Ichinohe S, Majima T, Mikami H, Niki Y, Tanaka S, Tsumura H
Value Health 2013; Regional Issue 2: 81-86

Health-related quality of life and productivity impact of myelodysplastic syndromes (MDS): The patient perspective
Komrokji R, Mahmoud D, Hudgens S, Taylor F, Pompilus F, Hwang S, Beach CL
Poster session presented at: 12th International Symposium on Myelodysplastic Syndromes, Berlin, 8-11 May 2013

Effectiveness of alcohol treatment interventions integrated into routine tuberculosis care in Tomsk, Russia
Shin S, Livchits V, Smith Connery H, Shields AL, Fitzmaurice G, Nelson A, Greenfield S
Addiction. 108(8),1387-1396

Training and fidelity monitoring of alcohol treatment interventions integrated into routine tuberculosis care in Tomsk, Russia: the IMPACT effectiveness trial
Smith Connery H, Greenfield SF, Livchits V, McGrady L, Patrick N, Lastimoso C, Hart J, Nelson AK, Shields AL et al. on behalf of the Tomsk Tuberculosis Alcohol Working Group
Substance Use and Misuse, 48(9):784-792

Health-related quality of life, treatment satisfaction, adherence and persistence in β-thalassemia and myelodysplastic syndrome patients with iron overload receiving deferasirox: Results from the EPIC clinical trial
Porter J, Bowden DK, Economou M, Gater A et al
Anemia, vol. 2012

Content validity of utility assessment in type 2 diabetes and Alzheimer’s disease
McGrath C, Rofail D, Abetz L
Qual Life Res 2010;19:29

Using qualitative methods to inform the trade-off between content validity and consistency in utility assessment: the example of type 2 diabetes and Alzheimer’s disease
McGrath C, Rofail D, Gargon E, Abetz L
Health Qual Life Outcomes 2010;8:23

Other publications

Informing a priori sample size estimation in qualitative concept elicitation interview studies for clinical outcome assessment instrument development
Turner-Bowker DM, Lamoureux RE, Stokes J, Litcher-Kelly L, Galipeau N, Yaworksy A, Solomon J, Shields AL
Value in Health

Evaluation of modified item characteristics on item comprehension and psychometric performance
Turner-Bowker DM, DeRosa M, Bjorner JB
Poster presented at the International Society for Pharmacoeconomics and Outcomes Research 23rd International Meeting, Baltimore MD, USA 19-23 May 2018.

Multi-comparator ICER: A new framework for cost-effectiveness analysis
Ratcliffe A, Lucherini S, Hughes R, Okhuoya P
Poster presented at the HTAi conference, Vancouver, Canada, 1-5 June 2018

Interpretation guidelines to define clinical relevance for patient-reported outcome (PRO) measures
Cocks K, Sully K, King M
Workshop presented at the International Society for Quality of Life Research (ISOQOL), Dublin, Ireland, 24-27 October 2018

Establishing anchor-based minimally important differences (MID) with the EORTC quality-of-life measures: a meta-analysis protocol
Musoro ZJ, Hamel J-F, Ediebah DE, Cocks K, King MT, Groenvold M, Sprngers MAG, Brandberg Y, Velikova G, Maringwa J, Flechtner H-H, Bottomley A, Coens C.
BMJ Open

Conducting qualitative ‘exit’ interviews following clinical trials or observational studies: a valuable method for understanding the patient experience, informing measurement strategy, and aiding interpretation of patient-reported outcomes
Arbuckle R, Carson RT, Maltzahn R, Staunton H
Workshop presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 22nd Annual International Meeting, Boston, US, 20-24 May 2017

Differences in vaccine pricing between high-income and low-income markets
Fadeyi I, McLean T, Tavella F, Heron L
Podium presentation at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 20th Annual European Congress, Glasgow, Scotland, 4-8 November 2017

The use of qualitative (exit) interviews in clinical trials: Value, implementation and key considerations
Gater A, Marshall C, Grant L, Wells J
Poster presented at International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 22nd Annual International Congress, Boston MA, USA, 20-24 May 2017

Development and validation of patient-reported outcome measures (PROMs): Selecting the most appropriate qualitative research methods to establish content validity
Grant L, Wells J, Kilgariff S, Marshall C, Gater A
Poster presented at the Advances in Patient Reported Outcomes Research Conference, 8 June 2017

Techniques for tailoring an interview guide for pediatric concept elicitation and cognitive debriefing interviews
Krohe M, Morrissey L, Turner-Bowker, DM
Poster session presented at the 22nd Annual International Meeting of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Boston, MA USA, 20-24 May 2017

How does measurement of multiple medication adherence differ between chronic diseases?
Malmenäs M, Pednekar P, Bennett B, Borah B
Forum presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 22nd Annual International Meeting, Boston, MA USA, 20-24 May 2017

A worked example of using computer-assisted qualitative data analysis software (CAQDAS) to support content validity in patient-centered outcomes research
Marshall C, Grant L, Wells J, Williamson N, Gater A
Poster presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 22nd Annual International Meeting, Boston, US, 20-24 May 2017

Qualitative research methods for collecting, analyzing, and presenting patient-reported data on noticeable and important change in disease-related signs and symptoms
Mazar I, Stokes J, Foley C, Galipeau N, Shields AL
Poster presented at  the 20th Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research. Glasgow, Scotland. 4-8 November

Saturation of sign and symptom concepts in concept elicitation studies with rare disease and vulnerable patient populations
Mazar I, Stokes J, Shields AL
Poster presented at the 22nd Annual International Meeting of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Boston, MA USA, 20-24 May 2017

Initiatives that impact pricing and reimbursement of orphan (and ultra orphan) drugs: Review of European trends
Rousseau B, Poinas AC, Oliver L, Collings H
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 20th Annual European Congress, Glasgow, Scotland, 4-8 November 2017

The use of intra-class correlation coefficients to assess test-retest reliabilities in psychometric evaluations of patient-reported outcome measures
Sen R, Yip C, Severson K
Poster submitted to the 20th Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research. Glasgow, Scotland. 4-8 November.

Techniques for the psychometric evaluation of clinical outcomes assessment (COA) measures used in rare disease
Turner-Bowker DM, Sen R, Morrissey L, Kelly M, Severson K, Litcher-Kelly L
24th Annual Conference of the International Society for Quality of Life Research

Assessing the joint probability of cost-effectiveness and affordability in decision making
Yi Y, Lucherini S, Bellanca L, Heron L
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 20th Annual European Congress, Glasgow, Scotland, 4-8 November 2017

Psychometric evaluation of a treatment acceptance measure for use in patients receiving treatment via subcutaneous injection
Tatlock S, Sanchez R, Grant L, Khan I, Manvelian G, Spertus J
Value Health. 2017 Mar;20(3):430-440

A patient-centred approach to developing patient-reported outcome measures (PROMs): Patients as research partners, not just participants
Panter C, Williamson N, Tatlock S, Hall R, Wells J, Gater A
Poster presented at: PROMs conference, Sheffield, UK, 9 June 2016

BEACON: A summary framework to overcome potential reimbursement hurdles
Dunlop W, Mullins D, Pirk O, Goeree R, Postma M, Enstone A, Heron L
macoEconomics (2016). doi:10.1007/s40273-016-0427-7

Challenges and solutions associated with patient-centered outcomes in rare diseases
Bonner N, Panter C, Spencer H, Braid J, Bennett B
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Washington DC, USA, 21-25 May 2016

Creating clinical outcome assessments on electronic platforms from the beginning: Challenges, consideration and advantages
Arbuckle R, Kilgariff S, Hall R, O’Donohoe P
Poster presented at ISOQOL, Copenhagen, Denmark, 19 – 22 October 2016

Empowering patient populations with physical or cognitive limitations through electronic clinical outcome assessments (eCOAs)
Tolley C, Garner K, Abel J
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Washington DC, USA, 21-25 May 2016

Exploring and leveraging known resources to support pediatric clinical outcomes assessment (COA) development
Turner-Bowker D, Krohe M, Banderas CA
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Washington DC, USA, 21-25 May 2016

Measuring multiple medication adherence – which measure when?
Pednekar P, Agh T, Malmenas M, Bennett B
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Vienna, Austria, 29th Oct-2nd Nov 2016

Patient reported outcomes status update on meaningful score changes to establish endpoint definitions: Challenges, observations, and (some) solutions from the field
Shields AL
Invited presentation for the DIA’s 3rd annual meeting on Advancing the Science of Study Endpoints. Washington DC, USA

Psychometric evaluation of clinical outcomes assessments in a phase II trial
Huang VW, Banderas B, Sen R
Poster presented at International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Vienna, Austria, 29th Oct-2nd Nov 2016

Simultaneous development of PRO questionnaires for use in clinical trials and ‘real-world’ situations
Shields A, Stokes J, Foley C, Banderas B, Sundaram M
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Washington DC, USA, 21-25 May 2016

Taking the ‘burden’ out of caregiver burden
Grant L, Kilgariff S, Hall R, Braid J, Bennett B
Pharmaphorum.com

The things kids say:  Clinical outcome assessments in pediatric clinical trials
Jackson C, Treem W, Turner-Bowker DM, Calarco G, Paty J, Mulberg A
Forum presentation at the DIA 2016 52nd Annual Meeting, Philadelphia, PA, June 26-30 2016

Understaning relationships between symptoms and impacts through a narrative analysis lens
Solomon J, Shields AL, Globe D, Foley C, Roy A, Pompiluus F, Yaworsky A, Ghate S, Perez JR
Poster presented at the 23rd Annual Conference of International Society for Quality of Life Research (ISOQOL); Copenhagen, Denmark

Web-based budget impact and pricing scenarios planning model: Example from the United Kingdom
Rousseau B, Johnson B, Topachevskyi O, Volovyk A
Value in Health 2016, Volume 19, Issue 3, A79

Web-based budget impact and pricing scenarios planning model: Example from the United Kingdom
Rousseau B, Johnson B, Topachevskyi O, Volovyk A
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Washington DC, USA, 21-25 May 2016

Best practice in health outcomes research
Bonner N
Pharmaphorum [Online] 2015

Developing and evaluating electronic clinical outcome assessments (eCOAs) for use in patient populations with substantial physical or cognitive limitations
Tolley C
eCOA Forum Scientific Sessions, Oxford, UK, 27th October 2015

Developing tools for use in clinical practice – a methodological approach
Tolley C, Hall R, Mills K, Bennett B
Poster session presented at International Society for Quality of Life Research (ISOQOL), 22nd Annual Conference, Vancouver, Canada, 21-24 October 2015

Development and content validity testing of a patient-reported treatment acceptance measure for use in patients receiving treatment via subcutaneous injection
Tatlock S, Grant L, Spertus J, Khan I, Arbuckle R, Manvelian G, Sanchez R
Value Health 2015;18;8:1000-1007

Development of evidence packages for regulatory and reimbursement submissions in rare diseases: real-world examples
Bonner N, Bowden A, Bal V, Kilburg A
Workshop presented at: 18th Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Milan, Italy, 7-11 November 2015

Development of patient-centered outcomes in rare diseases
Bonner N, MacCulloch A, Bennett B
Poster session presented at: World Orphan Drug Congress, Geneva, Switzerland, 11-13 November 2015

Digital methodologies in the development of clinical outcome assessments
Tolley C, Gater A, Marshall C, Dickie G, Kilgariff S
Poster session presented at International Society for Quality of Life Research (ISOQOL), 22nd Annual Conference, Vancouver, Canada, 21-24 October 2015

How many subjects are enough for symptom-focused concept elicitation studies? A retrospective analysis of saturation across twenty-six studies
Lamoureux R, Galipeau N, Yaworsky A, Stokes J, Shields AL
Poster session presented at: 20th Annual International Meeting of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), Philadelphia, PA, USA, 16-20 May 2015

Patient reported endpoints and the relevance to payers and regulators: Is there agreement?
Trask P, Bal V, Halling, K, Reasner D, Turpin R, Daniels S, Shields A
Invited panel at the 6th Annual Patient-reported Outcome Workshop. Silver Spring, MD USA

Telephone versus face-to-face interviews for patient-reported outcome instrument development
Mazar I, Lamoureux R, Ojo O, Kevane G, Banderas B, Stokes J, Shields A
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 18th Annual European Congress, Milan, Italy, 7-11 November 2015

Unique challenges in development, psychometric evaluation and interpretation of daily and event diaries as endpoints in clinical trials
Gater A, Coon CD, Nelsen LM, Girman C
Therapeutic Innovation and Regulatory Science 2015, 49(6): 813-821

Using classical test theory, item response theory, and Rasch measurement theory to evaluate patient-reported outcome measures: A comparison of worked examples
Petrillo J, Cano SJ, McLeod LD, Coon CD
Value in Health 2015;18(1):25-34

Clinical outcome assessment (COA) instrument scoring: The validity and precision of unweighted summary scores verse IRT weighted scores, and the added value of IRT standard errors
Coon CD, Lenderking WR
Poster presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 21st Annual International Meeting, Amsterdam, Netherlands, 8-12 November 2014

Development and validation of COA instruments as eCOA from the beginning: Advantages, opportunities and challenges
Gater A
Presentation at eCOA Forum Scientific Sessions, University of Oxford, 24-25 June 2014

Development of a patient-led end of study questionnaire to evaluate the experience of clinical trial participation
Brohan E, Bonner N, Turnbull A, Khan S, Dewit O, Thomas G, Manson S
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 17th Annual European Congress, Amsterdam, Netherlands, 8-12 November 2014

Development, validation and use of observer-reported outcomes in clinical trials: challenges and solutions
Patrick DL, Arbuckle R, Burke L
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 17th Annual European Congress, Amsterdam, Netherlands, 8-12 November 2014

Moving beyond the traditional psychometric validation of new phase 3 clinical outcome assessments
Kammerman LA, Izem R, Coon C, Johnson LL
Podium presentation at the Drug Information Association 50th Annual Meeting; June 2014. San Diego, CA

Informing drug development and clinical practice through patient-centered outcomes research
Coon CD, Lau DT
Clinical Therapeutics 2014;36(5):616-8

“Not just little adults”: Qualitative methods to support the development of pediatric patient-reported outcomes
Arbucke R, Abetz-Webb L
Patient 2013;6(3):143-59

A parent-administered but child-completed patient-reported outcome (PRO) provides a measure with content validity that is valid and reliable for use in children aged 6 to 11 years
Arbuckle R, Marshall C
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

Determining the magnitude of a detectable and a relevant treatment benefit in aesthetic medicine using a photoguide and the internet
Pleil AM, Bushmakin AG, Shields AL, Jensen J, Cappelleri JC
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

Evaluating and improving methods for cognitive debriefing PRO questionnaires
Stokes J, Yaworsky A, Galipeau N, Pompilus F, Foley C, Lamoureux R, Lovin R, Shields A
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 18th International Meeting, New Orleans, USA, 20 -22 May 2013

Exploratory structural equation models: A simulation study exploring geomin and target rotation techniques on variations of ESEM models
Sen R
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

How burdensome is completion of electronic patient-reported outcomes (ePRO)? Item completion times and qualitative evidence from studies in four different health conditions
Arbuckle R, Tolley C, Burbridge C
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

The development and validation of clinician-reported outcome instruments: The application of methods from patient-reported outcomes
Arbuckle R, Kitchen H, Tatlock S
Workshop presented at: 20th Annual Conference of the International Society for Quality of Life Research (ISOQOL), Miami, USA, October 9-12th, 2013

The effect of medical device dose-memory functions on patients’ adherence to treatment, confidence, and disease self-management
Hall R, Willgoss T, Humphrey L, Kongsø JH
Patient Prefer Adherence, 2013;8:775-788

The effect of medical devices with dose-memory and reminder functions on patients’ treatment adherence confidence and disease self-management
Hall R, Harald-Kongsø J, Humphrey L, Willgoss T
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

The use of creative exercises to maximise content drawn from concept elicitation interviews used to develop symptom and health-related quality of life measures in pediatric populations with chronic disease
Arbuckle R, Abetz-Webb L
Oral presentation presented at: 20th Annual Conference of the International Society for Quality of Life Research (ISOQOL), Miami, USA, October 9-12, 2013

The value of pilot testing PRO symptom diaries prior to conducting cognitive debriefing interviews in children/ adolescents: qualitative and quantitative insights
Arbuckle R, Holloway L, Carson RT, Dennee-Sommers B, Abetz-Webb L
Poster session presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR),  16th Annual European Congress, Dublin, Ireland, 2-6 November 2013

An interactive overview of using Computer-Assisted Qualitative Data Analysis Software (CAQDAS) in health outcomes research
Kitchen H, Marshall C
Workshop presented at: International Society for Quality of Life Research, 19th Annual Conference, Budapest, Hungary, 24–27 October 2012

Gaining reimbursement of orphan products in Europe: Challenges due to wide variations in evidence requirements and processes
Heron L, Laurenson S, Costello J, Anderl C, Knospe J
Value Health 2012;15:A308

Gaining reimbursement of orphan products in Europe: Challenges due to wide variations in evidence requirements and processes
Heron L, Laurenson S, Costello J, Anderl C, Knospe J
Poster presented at the 15th Annual European Congress of the International Society for Pharmacoeconomics and Outcomes Research (ISPOR). Berlin, Germany, 2012

Introduction to patient-reported outcomes
Crawford B, Yao K
Short course pressented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 5th Asia-Pacific Conference, Taipei, Taiwan, 2–4 September 2012

Evaluating the impact of patient recruitment and retention practices
Lamberti M J, Mathias A, Myles J, Howe D, Getz K
Drug Inf J 2012;46:573

Listening to children’s and parents’ voices: using patient-reported outcomes to empower patients with orphan diseases and their parents
Abetz-Webb A, Arbuckle R
Workshop presented at: 6th European Conference on Rare Diseases & Orphan Products, Brussels, Berlin, 23–25 May 2012

Listening to the patient: Using patient-reported outcomes to optimise adherence and inform healthcare decisions
Gater A
Journal For Patient Compliance Strategies to enhance Adherence and Health Outcomes. 2012; 2(2). 28-31

Pediatric patient-report outcomes and pediatric clinical trial design: Challenges and solutions
Arbuckle RA, Tassinari MS, Carson RT, Baird M
Workshop presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 17th Annual International Meeting, Washington, USA, 2–6 June 2012

Linguistic validation of translation of the Self-Assessment Goal Achievement (SAGA) questionnaire from English
Piault E, Doshi S, Brandt BA, Angün Ç, Evans CJ, Bergqvist A, Trocio J
Health Qual Life Outcomes 2012 23;10:40

Selection and development of clinical outcome assessments (COAs) for use in pediatric clinical trials
Tassinari MS, Wang P, Abetz L, Patrick D, Rofail, D, Lee J, Papadopoulos E
Oral presentation at Third Annual Patient-Reported Outcome Consortium workshop, Silver Spring, USA, 4 April 2012

Service user attachments to psychiatric key workers and teams
Arbuckle R, Berry K, Taylor JL
Soc Psychiatry Psychiatr Epidemiol 2012;47:817

Using Mapped EQ-5D from disease-specific measures in cost-utility analysis: What is the current state in Asia Pacific?
Leartsakulpanitch J, Crawford B, Lee EK, Chiou CF
Issue panel presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 5th Asia-Pacific Conference, Taipei, Taiwan, 2–4 September 2012

Pushing the boundaries of quality of life research: Using patients’ words in a gap analysis of PRO measures
Mukherjee Bal V, Lasch K
Qual Life Res 2012;20:13

Utilization of Rasch measurement models for assessing validity: A mixed methods approach
Hudgens S, Globe D, Burgess S M
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 17th Annual International Meeting, Washington, USA, 2–6 June 2012

‘Market access’ or just a new way of thinking about value?
Charlesworth B
Pharmaphorum 3 May 2011

Guidelines for pharmacoeconomic evaluation for Serbia
Novakovic T, Tesic D, Stefanovic D, Medic G, Sovtic D
Poster presented at the  International Society for Pharmacoeconomics and Outcomes Research (ISPOR). Madrid, Spain, 2011

Paediatrics: An unexplored and rewarding population – the right methods make it easier
Abetz L
Pharmaphorum 28 July 2011

The impact of regulatory (FDA and EMA) and EUNETHTA guidelines on patient-reported outcomes and health-related quality of life on market authorisation and pricing
Arnould B, Symonds T, Trueman P, Pavlovic M, Abetz L
Issue panel presented at the  International Society for Pharmacoeconomics and Outcomes Research (ISPOR). Madrid, Spain, 2011

The value of medicine: opportunities, not threats
Charlesworth B
Pharmaphorum 10 June 2011

The role of health-related quality of life data in the drug approval processes in the United States and Europe: a review of guidance documents and authorizations of medicinal products from 2006 to 2010
Marquis P, Caron M, Emery M P, Scott J, Arnould B, Acquadro C
Pharm Med 2011; 25:147

Value Based Health Care Working Group
Naci H
Workshop presented at the  International Society for Pharmacoeconomics and Outcomes Research (ISPOR). Madrid, Spain, 2011

Treatment satisfaction instruments for different purposes during a product’s lifecycle: Keeping the end in mind
Rofail D, Regnault A, Taylor F, Filonenko A
Patient.  2011;4(4):22

An introduction to pediatric patient-reported outcomes and pediatric clinical trial design
Arbuckle R, Abetz-Webb L, Carson R, Edelman Lewis B, Chassany O
Workshop presented at the International Society for Quality of Life Research 17th Annual Conference, London, UK, 27–30 October 2010

Conducting outcomes research in Asia: Challenges of local adaptation of global OR studies
Crawford B, Wang L, Leartsakulpanitch J
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 4th Asia-Pacific Conference, Phuket, Thailand, 5–7 September 2010

Health care data in Asia: Collecting, sharing and using
Bae S, Pwu RF, Xu L, Srithamrongsawat S, Ikdea S, Aljunid S, Bhattacharjya A, Crawford B, Sung J
Plenary session at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 4th Asia-Pacific Conference, Phuket, Thailand, 5–7 September 2010

PRO development: Rigorous qualitative research as the crucial foundation
Lasch KE, Marquis P, Vigneux M, Abetz L, Arnould B, Bayliss M, Crawford B, Rosa K
Qual Life Res 2010;19(8):1087-1096

Psychometric validation of the ascites impact measure questionnaire to assess patient symptoms that trigger a paracentesis
Piault E, Yeh Y, Crawford B, Joulain F, Gotlieb W
Qual Life Res 2010;19:116

The missing piece between treatment experience and intention to persist: Testing the internal consistency reliability and predictive validity of acceptability
Viala-Danten M
Poster presented at ISPOR 13th Annual European Congress, 6-9 November 2010, Prague, Czech Republic

Treatment satisfaction instruments for different purposes during a product’s lifecycle: Keeping the end in mind
Rofail D, Regnault A, Taylor F, Filonenko A
Poster session presented at ISPOR 13th Annual European Congress, Prague, 6-9 November 2010

Using population-based data in outcomes research studies: Strengths, weaknesses and lessons learned
Chen W, Tang CH, Crawford B, Sung J
Workshop presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 4th Asia-Pacific Conference, Phuket, Thailand, 5–7 September 2010

Advanced patient-reported outcomes assessment: Psychometric methods
Crawford B, Rosa K, McDonald J
Short course presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 14th Annual International Meeting, Orlando,  USA, 16–19 May 2009

Strategy and guidelines for conducting and analyzing patient-reported outcomes in clinical trials
Crawford B, Rosa K, McDonald J
Short course presented at: International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 14th Annual International Meeting, Orlando, USA, 16–19 May 2009

Medical savings accounts in China
Yi Y, Maynard A
Euro Observer 2008; 10(4):12-14

The significance of patient-reported outcomes to facilitate market access during a product’s lifecycle
Rofail D, Abetz A, Gater A, Brown C
Presented at the International Society for Pharmacoeconomics and Outcomes Research (ISPOR), 11th Annual Congress, Athens, 8–11 November 2008